Canlyniadau Chwilio - An Haack, Kristina

Screening for calcium channel modulators in CLN3 siRNA knock down SH-SY5Y neuroblastoma cells reveals a significant decrease of intracellular calcium levels by selected L-type calc... gan an Haack, Kristina, Narayan, Srinivas B., Li, Haying, Warnock, Ashley, Tan, Lu, Bennett, Michael J.

Cael y testun llawn Cael y testun llawn Cael y testun llawn

Qualitative interviews to improve patient-reported outcome measures in late-onset Pompe disease: the patient perspective gan Hamed, Alaa, An Haack, Kristina, Gwaltney, Chad, Baranowski, Eileen, Stewart, Andrew, Krupnick, Robert, Tyler, Margaret, Sparks, Susan, Paty, Jean

Cael y testun llawn Cael y testun llawn Cael y testun llawn

Forced vital capacity and cross-domain late-onset Pompe disease outcomes: an individual patient-level data meta-analysis gan Berger, Kenneth I., Kanters, Steve, Jansen, Jeroen P., Stewart, Andrew, Sparks, Susan, Haack, Kristina An, Bolzani, Anna, Siliman, Gaye, Hamed, Alaa

Cael y testun llawn Cael y testun llawn Cael y testun llawn

Development and content validation of the Pediatric Oral Medicines Acceptability Questionnaires (P-OMAQ): patient-reported and caregiver-reported outcome measures gan Turner-Bowker, Diane M., An Haack, Kristina, Krohe, Meaghan, Yaworsky, Andrew, Vivas, Norma, Kelly, Masami, Chatterjee, Godhuli, Chaston, Emily, Mann, Erin, Reaney, Matthew

Cael y testun llawn Cael y testun llawn Cael y testun llawn

How is the Pharmaceutical Industry Structured to Optimize Pediatric Drug Development? Existing Pediatric Structure Models and Proposed Recommendations for Structural Enhancement gan Severin, Thomas, Corriol-Rohou, Solange, Bucci-Rechtweg, Christina, an Haack, Kristina, Fuerst-Recktenwald, Sabine, Lepola, Pirkko, Norjavaara, Ensio, Dehlinger-Kremer, Martine, Haertter, Sebastian, Cheung, S. Y. Amy

Cael y testun llawn Cael y testun llawn Cael y testun llawn

Correction to: How is the Pharmaceutical Industry Structured to Optimize Pediatric Drug Development? Existing Pediatric Structure Models and Proposed Recommendations for Structural... gan Severin, Thomas, Corriol-Rohou, Solange, Bucci-Rechtweg, Christina, an Haack, Kristina, Fuerst-Recktenwald, Sabine, Lepola, Pirkko, Norjavaara, Ensio, Dehlinger-Kremer, Martine, Haertter, Sebastian, Cheung, S. Y. Amy

Cael y testun llawn Cael y testun llawn Cael y testun llawn

Clinical characteristics and genotypes in the ADVANCE baseline data set, a comprehensive cohort of US children and adolescents with Pompe disease gan Kishnani, Priya S., Gibson, James B., Gambello, Michael J., Hillman, Richard, Stockton, David W., Kronn, David, Leslie, Nancy D., Pena, Loren D. M., Tanpaiboon, Pranoot, Day, John W., Wang, Raymond Y., Goldstein, Jennifer L., An Haack, Kristina, Sparks, Susan E., Zhao, Yang, Hahn, Si Houn

Cael y testun llawn Cael y testun llawn Cael y testun llawn

Characterization of Early Disease Status in Treatment-Naive Male Paediatric Patients with Fabry Disease Enrolled in a Randomized Clinical Trial gan Wijburg, Frits A., Bénichou, Bernard, Bichet, Daniel G., Clarke, Lorne A., Dostalova, Gabriela, Fainboim, Alejandro, Fellgiebel, Andreas, Forcelini, Cassiano, An Haack, Kristina, Hopkin, Robert J., Mauer, Michael, Najafian, Behzad, Scott, C. Ronald, Shankar, Suma P., Thurberg, Beth L., Tøndel, Camilla, Tylki-Szymańska, Anna, Ramaswami, Uma

Cael y testun llawn Cael y testun llawn Cael y testun llawn